Hemophilia Gene Therapy: Advancements, Challenges, and Future Prospects
Abstract Hemophilia, a genetic disorder characterized by the inability of blood to clot properly, affects thousands globally, necessitating long-term treatment strategies. Traditional therapies, while effective, demand regular administration, posing a challenge to patients. Gene therapy emerges as a promising approach to potentially cure hemophilia by addressing its genetic root cause. This paper explores the advancements, …